Translating Science. Transforming Lives.

PTC Therapeutics Limited, a subsidiary of PTC Therapeutics, Inc, is an integrated biopharmaceutical company based on expertise in RNA biology. We have focused on discovering and developing novel oral treatments for patients with serious and life-limiting disorders. By targeting the processes that modulate RNA biology and affect protein production, we bring an innovative approach to drug discovery. We are focused particularly on the development and commercialization of treatments for rare and neglected disorders. We work closely with specialist physicians, nurses, pharmacists and other healthcare professionals to develop and market medicines that aim to improve quality of life for patients and their families.

Commitment to Patients.

We are committed to finding treatment options for patients with life-threatening diseases.

A Message From Our CEO

Stuart W. Peltz, Ph.D. During grad school, I was always interested in science and biology so I chose to focus my efforts in RNA biology regulation. At the time this was an area that was not well understood, making it a new and exciting field. Concentrating in this area, I felt, would impact our understanding of how basic biology works, which as a consequence would be important for the development of new medicines.

As a professor at Rutgers Robert Wood Johnson Medical School in New Jersey, I had the opportunity to further my research in the area of post transcriptional control of gene expression of RNA. Along the way I realized that translating scientific efforts into medicines requires many people with an incredible amount of expertise in multiple disciplines. And that’s how PTC was born.

Working in orphan diseases like Duchenne muscular dystrophy and spinal muscular atrophy positions you right in front of the patients and their families. You have the opportunity to understand the challenges that these families face every day. The possibility of leading the team that tries to discover drugs that alter the course of these diseases and hopefully change the lives of these patients gives our work incredible purpose; it inspires and motivates all of us at PTC. It helps everyone understand why we are always so persistent; every day matters to the patients and their families. It makes PTC a cause as much as a company.

Founding this biotech company has exceeded my expectations of what happens when you get all the right ingredients together. We have been fortunate to have an outstanding team; we are a family. We’ve celebrated the good times and worked through the challenging times. At PTC, you will find our employees embody perseverance and most importantly believe in the shared vision of doing great science, with the goal of bringing new potential treatments to patients.

As a professor at UMDNJ, I had a vision for a company. One that is made up of talented, driven individuals focused each day on applying great science to develop new treatments that may change the course of disease and address unmet medical needs. As you learn more about our company, I hope you get a sense of our commitment to the patients and to developing treatments for rare and neglected diseases.



Stuart Peltz, Ph.D.

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